How can gene-editing of human pluripotent stem cells help cystic fibrosis?
(2019)
Presentation / Conference Contribution
Cuevas Ocana, S., Wong, A., Aushev, M., Ye Yang, J., Perkins, N., Bear, C., …Gray, M. (2019). How can gene-editing of human pluripotent stem cells help cystic fibrosis?. European Respiratory Journal, 54(suppl 63), Article OA2125. https://doi.org/10.1183/13993003.congress-2019.oa2125
Cystic fibrosis (CF) is a monogenic recessive disorder, affecting 70,000 people worldwide. CF is due to mutations in the CFTR gene, resulting in a defective protein that leads to symptoms in numerous organs, especially lungs. Despite recent advances,... Read More about How can gene-editing of human pluripotent stem cells help cystic fibrosis?.