How can gene-editing of human pluripotent stem cells help cystic fibrosis?
(2019)
Journal Article
Cuevas Ocana, S., Wong, A., Aushev, M., Ye Yang, J., Perkins, N., Bear, C., …Gray, M. (2019). How can gene-editing of human pluripotent stem cells help cystic fibrosis?. European Respiratory Journal, 54(suppl 63), Article OA2125. https://doi.org/10.1183/13993003.congress-2019.oa2125
Cystic fibrosis (CF) is a monogenic recessive disorder, affecting 70,000 people worldwide. CF is due to mutations in the CFTR gene, resulting in a defective protein that leads to symptoms in numerous organs, especially lungs. Despite recent advances,... Read More about How can gene-editing of human pluripotent stem cells help cystic fibrosis?.